What is Palynziq (pegvaliase-pqpz), and how does it work? Palynziq (pegvaliase-pqpz) is a prescription medicine used to lower blood levels of phenylalanine in adults with PKU (phenylketonuria) who have uncontrolled blood phenylalanine levels above 600 micromol/L (10 mg/dL) on their current treatment. It is not known if Palynziq is safe and effective in children. Palynziq …
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What is Alkindi Sprinkle (hydrocortisone), and how does it work? Alkindi Sprinkle contains a drug called hydrocortisone. Hydrocortisone belongs to a group of medicines known as corticosteroids. Hydrocortisone is a synthetic version of the hormone cortisol. Cortisol is made naturally by the adrenal glands in the body. Alkindi Sprinkle is a prescription medicine that contains hydrocortisone also called a corticosteroid. …
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What is Sogroya, and how does it work? Sogroya is indicated for the replacement of endogenous growth hormone (GH) in adults with growth hormone deficiency (GHD). Sogroya is a prescription medicine that contains human growth hormone, the same growth hormone made by the human body. Sogroya is given by injection under the skin (subcutaneous) and is used to treat adults …
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What is Injectafer (ferric carboxymaltose), and how does it work? Injectafer is a prescription iron replacement medicine used to treat iron deficiency anemia (IDA) in adults who have: intolerance to oral iron or who have not responded well to treatment with oral iron, or non-dialysis dependent chronic kidney disease It is not known if Injectafer is safe and effective for …
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What is Monoferric (ferric derisomaltose), and how does it work? Monoferric is a prescription iron replacement medicine used to treat iron deficiency anemia in adults who have: intolerance to oral iron or who have not responded well to treatment with oral iron non-dialysis dependent chronic kidney disease It is not known if Monoferric is safe and effective for use in …
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What is Galafold and how does it work? Galafold is a prescription medicine used to treat adults with Fabry disease who have a certain genetic change (variant) in the galactosidase alpha gene (GLA) that is responsive (amenable) to Galafold. It is not known if Galafold is safe and effective in children. What are the side effects of Galafold? The most …
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What is Ilaris (canakinumab), and how does it work? Ilaris is a prescription medicine injected by your healthcare provider just below the skin (subcutaneous) used to treat: The following Periodic Fever Syndromes Adults and children 4 years of age and older who have auto-inflammatory diseases called Cryopyrin-Associated Periodic Syndromes (CAPS), including: Familial Cold Auto-inflammatory Syndrome (FCAS) Muckle-Wells Syndrome (MWS) Adults …
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What is Venofer (iron sucrose), and how does it work? Venofer (iron sucrose) Injection is an iron replacement product used to treat iron deficiency anemia in people with kidney disease. Venofer is usually given with another medication to promote the growth of red blood cells (such as Aranesp, Epogen, or Procrit). Venofer is indicated for the treatment of iron deficiency …
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What is Feraheme (ferumoxytol injection), and how does it work? Feraheme is a prescription medicine used to treat iron deficiency anemia in adults who have: intolerance to oral iron or who have not responded well to treatment with oral iron or chronic kidney disease (CKD) It is not known if Feraheme is safe and effective in children less than 18 …
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What is Fludeoxyglucose and how does it work? Fludeoxyglucose F 18 Injection (fdg) is a positron emitting radiopharmaceutical used for diagnostic purposes in conjunction with Positron Emission Tomography (PET). It is also used to assist assessment of cancer, coronary artery disease, or epileptic seizures. Fludeoxyglucose F 18 Injection,USP is indicated in PET (positron emission tomography) for: Identification of regions of abnormal …
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